Day 1 of the 2001 AMDA POMPE Conference in San Antonio, TX on September 29, 2001.
0:00 Welcome - Randall H. House; President of AMDA
03:30 Overview of Developments in Pompe’s Disease - J.J. Reuser, Ph.D.; (Associate Professor of Cell Biology, Department of Clinical Genetics, Erasmus University, Rotterdamn, the Netherlands)
35:17 Enzyme therapy for Pompe's Disease with recombinant human alpha-glucosidase from rabbit milk - Ans T. van der Ploeg, M.D., Ph.D; (Department of Neonatology, Sophia Children's Hospital, Rotterdam, the Netherlands)
1:05:10 Therapy for patients with Pompe Disease: Enzyme Replacement Therapy Gene Transfer Strategies - Andrea Amalfitano, D.O., Ph.D (Assistant Professor Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA)
1:35:50 Question and Answer Session - Ans T. van der Ploeg, M.D., Ph.D; (Department of Neonatology, Sophia Children's Hospital, Rotterdam, the Netherlands) and Andrea Amalfitano, D.O., Ph.D (Assistant professor Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA)
2:03:19 Enzyme Replacement Therapy In Infantile Pompe Disease - Lars Klinge, M.D., (University Children't Hospital, Essen, Germany)
Website:
https://amda-pompe.org/

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