Repairing the Underlying Cause of Rett Syndrome Through RNA Editing | Rett Syndrome Research Trust |
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Drs. Gail Mandel and John Sinnamon discuss how RNA editing works, which MECP2 mutations can be edited and what the next steps are to develop this technology into a therapeutic for Rett Syndrome.
--------------------------------- The Rett Syndrome Research Trust is singularly focused on a cure for Rett syndrome. Achieving success takes a deep understanding of the relevant science, an environment built for scientific collaboration, and experience with drug and business development. Today we are building on incredible scientific and industry momentum by implementing six genetic-based strategies that tackle Rett from every angle. Every single company pursuing a cure for Rett is able to do so because they leveraged discoveries and resources that were generated with RSRT funding. RSRT is the home of the Rett cure community, and we are confident that together we will cure Rett syndrome. |